A new gene therapy turns glial cells—abundant support cells in the brain—into neurons, repairing damage that results from stroke and significantly improving motor function in mice. A paper d... Read more
Breakthrough research shows that stem cell genes can be edited in living systems New research led by Harvard scientist Amy Wagers has demonstrated that gene-editing machinery can be delivere... Read more
New data shows patients maintaining vision after a single intravitreal injection of gene therapy Gene therapy is showing promise for one of the most common causes of blindness. Data presen... Read more
Researchers from the Netherlands Institute for Neuroscience (NIN) and the Leiden University Medical Center (LUMC) have shown that treatment using gene therapy leads to a faster recovery afte... Read more
Treatment Uses Reduced-Intensity Preconditioning to Enhance Its Global Transportability After over a decade of preclinical research and development, a new gene therapy treatment for sickle c... Read more
Biological engineers design RNA circuits that enable precise control over the dose of therapeutic protein a patient receives. Delivering functional genes into cells to replace mutated genes,... Read more
