Treatment Uses Reduced-Intensity Preconditioning to Enhance Its Global Transportability After over a decade of preclinical research and development, a new gene therapy treatment for sickle c... Read more
Scientists have successfully used gene editing to repair 20 to 40 percent of stem and progenitor cells taken from the peripheral blood of patients with sickle cell disease, according to Rice... Read more
Bioengineer Gang Bao uses gene editing to repair up to 40 percent of bone marrow cells from patients Scientists have successfully used gene editing to repair 20 to 40 percent of stem and pro... Read more
A team of physicians and laboratory scientists has taken a key step toward a cure for sickle cell disease, using CRISPR-Cas9 gene editing to fix the mutated gene responsible for the disease... Read more
An established drug for recurrent multiple myeloma might effectively be repurposed to improve the survival and day-to-day lives of patients with devastating sickle cell disease, according to... Read more
Physicians at the University of Illinois Hospital & Health Sciences System have cured 12 adult patients of sickle cell disease using a unique procedure for stem cell transplantation from... Read more