Gene Therapy

CRISPR-Cas9 and other gene editing systems may need to be customized to the patient

Patients’ individual genomes may affect efficacy, safety of gene editing Gene editing has begun to

Gene therapy can restore vision to people with an inherited retinal disorder

Study shows first-of-its kind gene therapy can restore vision to people with an inherited retinal

Gene therapy can cure lameness in horses – big implications

Injecting DNA into injured horse tendons and ligaments can cure lameness, new research involving scientists

Preserving the vision of people with wet age-related macular degeneration (AMD) with a new and safe gene therapy

In a small and preliminary clinical trial, Johns Hopkins researchers and their collaborators have shown

A single gene therapy treatment could give life-long protection from severe allergies such as asthma

Gene therapy could ‘turn off’ severe allergies A single treatment giving life-long protection from severe

A way to curb chronic pain by modulating genes that reduce tissue and cell damaging inflammation

  For millions of sufferers, there is nothing more debilitating than chronic back or joint

Hearing restored down to a whisper in deaf mice via gene therapy

In the summer of 2015, a team at Boston Children’s Hospital and Harvard Medical School

New gene-editing technology open new treatment possibilities for retinal, heart and neurological diseases

Salk researchers have discovered, for the first time, how to place DNA in specific locations

Gene therapy in a droplet could treat eye diseases, prevent blindness

Eye diseases such as diabetic retinopathy and age-related macular degeneration are among the leading causes

Scientist develops gene therapy for muscle wasting

A discovery by Washington State University scientist Dan Rodgers and collaborator Paul Gregorevic could save

Gene helps prevent heart attack, stroke — and may offer way to block effects of aging

A gene that scientific dogma insists is inactive in adults actually plays a vital role

Drug ‘cocktail’ plus gene therapy could restore vision in optic nerve injury

Channel blocker drug, added to regenerative factors, is key Research from Boston Children’s Hospital suggests

Possible Vision Restoration for Macular Degeneration Sufferers

Millions of adults over age 50 struggle each year with vision loss caused by damage

Gene Therapy Treats All Muscles in the Body in Muscular Dystrophy Dogs; Human Clinical Trials Are Next Step

Muscular dystrophy, which affects approximately 250,000 people in the U.S., occurs when damaged muscle tissue

Mapping the Genes that Increase Lifespan

Following an exhaustive, ten-year effort, scientists at the Buck Institute for Research on Aging and