Gene Therapy
A new gene therapy turns glial cells—abundant support cells in the brain—into neurons, repairing damage
Successful T cell engineering with gene scissors The idea of genetically modifying a patient’s own
Breakthrough research shows that stem cell genes can be edited in living systems New research
The research group led by Prof. Alex Schier, Director of the University of Basel’s Biozentrum,
Researchers from the Netherlands Institute for Neuroscience (NIN) and the Leiden University Medical Center (LUMC)
Treatment Uses Reduced-Intensity Preconditioning to Enhance Its Global Transportability After over a decade of preclinical
Biological engineers design RNA circuits that enable precise control over the dose of therapeutic protein
Researchers at King’s College London have shown that rats with spinal cord injuries can re-learn
As scientists gain insights into which genes drive diseases, they are pursuing the next logical
Researchers from Drexel University reversed symptoms of Alzheimer’s disease in fruit flies by restoring the balance between
The results could open the door to new targeted therapies for this debilitating disease in
Researchers from the University of Pennsylvania have developed a gene therapy that successfully treats a form of
Type 1 diabetes is a chronic disease in which the immune system attacks and destroys
FINDINGS Through gene therapy, researchers engineered blood-forming stem cells (hematopoietic stem/progenitor cells, or HSPCs) to
A ‘cure’ for haemophilia is one step closer, following results of a groundbreaking gene therapy